Answer
It is licensed for people with cystic fibrosis who have F508del on both copies of the CFTR gene. The licensed formulation depends on age and, for younger children, weight.
Sources for this answer
- Orkambi 150 mg/188 mg granules in sachet — Current selected SmPCemc · Summary of Product Characteristics
- Orkambi 200 mg/125 mg film coated tablets — Current selected SmPCemc · Summary of Product Characteristics
General medicine information. Follow the instructions for your own medicine and speak to a pharmacist or clinician about your individual circumstances.