miglustat · Medicine question

What is miglustat used for?

iatroX medicinesPublished 21 August 2026Reviewed 21 August 2026

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The selected product treats mild to moderate type 1 Gaucher disease in adults when enzyme replacement therapy is unsuitable, and progressive neurological manifestations of Niemann–Pick type C disease in adults and children.

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Yargesa (miglustat) 100mg Hard Capsulesemc · SmPC Current selected SmPC · Version 6

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Is miglustat an enzyme replacement therapy?Can miglustat be taken with food?What should I do if miglustat causes persistent diarrhoea?Can miglustat affect the nerves?Can miglustat be used during pregnancy or breastfeeding?Is miglustat suitable for people with kidney problems?

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