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Medicines miglustatQuestion & answer

miglustat · Medicine question

Is miglustat an enzyme replacement therapy?

iatroX medicinesPublished 21 August 2026Reviewed 21 August 2026

The answer

Answer

No. It is substrate-reduction therapy that decreases production of certain glycosphingolipids.

Sources for this answer

Yargesa (miglustat) 100mg Hard Capsulesemc · SmPC Current selected SmPC · Version 6

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The full medicine guide

miglustat

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Read the miglustat guide

More questions about miglustat

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