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Medicines onasemnogene abeparvovecQuestion & answer

onasemnogene abeparvovec · Medicine question

What is onasemnogene abeparvovec used for?

iatroX medicinesPublished 21 August 2026Reviewed 21 August 2026

The answer

Answer

It treats specified forms of 5q spinal muscular atrophy caused by bi-allelic SMN1 mutations.

Sources for this answer

Zolgensma 2 x 10Exp13 vector genomes/mL solution for infusionemc · SmPC Current selected SmPC · Version 16

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The full medicine guide

onasemnogene abeparvovec

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More questions about onasemnogene abeparvovec

How does it help spinal muscular atrophy?Does it cure spinal muscular atrophy?Why are blood tests needed after treatment?Can vaccines be given around treatment?

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