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Medicines onasemnogene abeparvovecQuestion & answer

onasemnogene abeparvovec · Medicine question

How does it help spinal muscular atrophy?

iatroX medicinesPublished 21 August 2026Reviewed 21 August 2026

The answer

Answer

It delivers a functional SMN1 gene so motor neurons can make more survival motor neuron protein.

Sources for this answer

Zolgensma 2 x 10Exp13 vector genomes/mL solution for infusionemc · SmPC Current selected SmPC · Version 16

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onasemnogene abeparvovec

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More questions about onasemnogene abeparvovec

What is onasemnogene abeparvovec used for?Does it cure spinal muscular atrophy?Why are blood tests needed after treatment?Can vaccines be given around treatment?

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