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Medicines atidarsagene autotemcelQuestion & answer

atidarsagene autotemcel · Medicine question

What is atidarsagene autotemcel used for?

iatroX medicinesPublished 18 August 2026Reviewed 18 August 2026

The answer

Answer

It treats selected children with late-infantile or early-juvenile metachromatic leukodystrophy caused by faulty ARSA genes.

Sources for this answer

Libmeldyemc · SmPC Current selected SmPC · Version 4

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The full medicine guide

atidarsagene autotemcel

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More questions about atidarsagene autotemcel

Can it be used after symptoms begin?How is it made?How is it given?What are the main short-term risks?Can it cause HIV infection?Can a child have vaccines around treatment?

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