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Medicines atidarsagene autotemcelQuestion & answer

atidarsagene autotemcel · Medicine question

How is it made?

iatroX medicinesPublished 18 August 2026Reviewed 18 August 2026

The answer

Answer

Blood-forming stem cells are collected from the child and genetically modified in a laboratory to carry a functional ARSA gene.

Sources for this answer

Libmeldyemc · SmPC Current selected SmPC · Version 4

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The full medicine guide

atidarsagene autotemcel

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