Answer
Elaprase (idursulfase) is used for long-term treatment of Hunter syndrome (mucopolysaccharidosis II, MPS II); heterozygous females were not studied in clinical trials.
Sources for this answer
- Elaprase 2 mg/ml concentrate for solution for infusionTakeda UK Ltd · emc · SmPC §4.1 Therapeutic Indications · Version 21Document updated
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