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Medicines eladocagene exuparvovecQuestion & answer

eladocagene exuparvovec · Medicine question

Is eladocagene exuparvovec a gene therapy?

iatroX medicinesPublished 20 August 2026Reviewed 20 August 2026

The answer

Answer

Yes. It uses a modified, non-replicating AAV2 vector to deliver a functioning DDC gene to brain cells.

Sources for this answer

Upstaza (Eladocagene exuparvovec) solution for infusionemc · SmPC Current selected SmPC · Version 7

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The full medicine guide

eladocagene exuparvovec

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Read the eladocagene exuparvovec guide

More questions about eladocagene exuparvovec

How is it administered?Does treatment remove every symptom of AADC deficiency?Can a treated person donate blood or organs?Why is long-term follow-up needed?

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