Answer
Eligibility requires vision loss from inherited retinal dystrophy, confirmed harmful mutations in both RPE65 gene copies and enough viable retinal cells to treat. Assessment is undertaken by a specialist inherited-retinal-disease team.
Sources for this answer
- Luxturna concentrate and solvent for solution for injection — Current selected SmPCemc · Summary of Product Characteristics
General medicine information. Follow the instructions for your own medicine and speak to a pharmacist or clinician about your individual circumstances.