voretigene neparvovec · Medicine question

Who is eligible for voretigene neparvovec?

iatroX medicinesPublished 22 August 2026Reviewed 22 August 2026

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Eligibility requires vision loss from inherited retinal dystrophy, confirmed harmful mutations in both RPE65 gene copies and enough viable retinal cells to treat. Assessment is undertaken by a specialist inherited-retinal-disease team.

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