Answer
Hemgenix (etranacogene dezaparvovec) uses a non-replicating recombinant adeno-associated viral vector of serotype 5 (AAV5) to deliver coding DNA for the human Factor IX Padua variant to liver cells.
Sources for this answer
- HemgenixCSL Behring UK Limited · emc · SmPC §5.1 Pharmacodynamic properties · Version 8Document updated
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