Answer
Cystadane (betaine anhydrous) is indicated as adjunctive treatment of homocystinuria involving deficiencies or defects in cystathionine beta-synthase (CBS), 5,10-methylene-tetrahydrofolate reductase (MTHFR), or cobalamin cofactor metabolism (cbl), supplementing other therapies.
Sources for this answer
- Cystadane 1 g oral powderRecordati Rare Diseases UK Ltd · emc · SmPC §4.1 Therapeutic Indications · Version 12Document updated
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