Answer
Sapropterin dihydrochloride is indicated to treat hyperphenylalaninaemia in adults and paediatric patients of all ages with phenylketonuria or tetrahydrobiopterin (BH4) deficiency who have been shown to respond to treatment.
Sources for this answer
- Sapropterin dihydrochloride 100 mg Soluble TabletsTeva UK Limited · emc · SmPC §4.1 Therapeutic Indications · Version 1Document updated
Sources checked