Answer
Subretinal injection of voretigene neparvovec transduces retinal pigment epithelial cells with cDNA encoding normal human RPE65 protein, providing the potential to restore the visual cycle through gene augmentation therapy.
Sources for this answer
- Luxturna concentrate and solvent for solution for injectionNovartis Pharmaceuticals UK Ltd · emc · SmPC §5.1 Pharmacodynamic properties · Version 9Document updated
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