Answer
Vestronidase alfa provides recombinant human beta-glucuronidase, the enzyme deficient in MPS VII, for uptake into cellular lysosomes and breakdown of accumulated glycosaminoglycans in affected tissues.
Sources for this answer
- Mepsevii 2 mg/mL concentrate for solution for infusionUltragenyx UK · emc · SmPC §5.1 Pharmacodynamic properties · Version 1Document updated
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