Answer
After intravenous infusion, agalsidase beta enters lysosomes in vascular endothelial and parenchymal cells, restoring enzyme activity to clear accumulated GL-3, with the aim of preventing, stabilising or reversing organ-function decline before irreversible damage occurs.
Sources for this answer
- Fabrazyme 35mg powder for concentrate for solution for infusionSANOFI · emc · SmPC §5.1 Pharmacodynamic properties · Version 2Document updated
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