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Medicines risdiplamQuestion & answer

risdiplam · Medicine question

Does risdiplam cure spinal muscular atrophy?

iatroX medicinesPublished 21 August 2026Reviewed 21 August 2026

The answer

Answer

No. It increases functional SMN protein but does not correct the underlying genetic change or reverse all existing damage.

Sources for this answer

Evrysdi 0.75 mg/mL powder for oral solutionemc · SmPC Current selected SmPC · Version 12
Evrysdi 5 mg film‑coated tabletsemc · SmPC Current selected SmPC · Version 1
NHS

NHS · NHS medicine guidance

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risdiplam

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