Answer
It is not a cure. It aims to increase production of full-length dystrophin, while multidisciplinary Duchenne care remains necessary.
Sources for this answer
- Translarna 125 mg granules for oral suspension — Current selected SmPCemc · Summary of Product Characteristics
- NHSNHS · NHS medicine guidance
General medicine information. Follow the instructions for your own medicine and speak to a pharmacist or clinician about your individual circumstances.