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Medicines atalurenQuestion & answer

ataluren · Medicine question

Does ataluren cure Duchenne muscular dystrophy?

iatroX medicinesPublished 18 August 2026Reviewed 18 August 2026

The answer

Answer

It is not a cure. It aims to increase production of full-length dystrophin, while multidisciplinary Duchenne care remains necessary.

Sources for this answer

Translarna 125 mg granules for oral suspensionemc · SmPC Current selected SmPC · Version 23
NHSNHS · NHS medicine guidance

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ataluren

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More questions about ataluren

Does ataluren work for every dystrophin-gene mutation?Is genetic testing required?Can the granules be mixed with food?Can antibiotics be given with ataluren?How can a suspected side effect be reported?